• FDA approves new treatment option for patients with rare Duchenne muscular dystrophy mutation

    1 month ago - By News Medical

    Today, the U.S. Food and Drug Administration granted accelerated approval to Viltepso injection for the treatment of Duchenne muscular dystrophy in patients who have a confirmed mutation of the DMD gene that is amenable to exon 53 skipping.
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  • FDA OKs Viltolarsen for Duchenne Muscular Dystrophy

    1 month ago - By Medscape

    Viltolarsen is for patients with Duchenne muscular dystrophy with a confirmed mutation amenable to exon 53 skipping.
    FDA Approvals
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  • Rare Duchenne Muscular Dystrophy Mutation Has New Tx

    Rare Duchenne Muscular Dystrophy Mutation Has New Tx

    1 month ago - By MedPageToday

    WASHINGTON - Viltolarsen injection has been approved to treat Duchenne muscular dystrophy in patients with a confirmed mutation in the DMD gene amenable to exon 53 skipping, the FDA said Wednesday.
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