• FDA OKs First Gene Therapy for Beta-Thalassemia

    1 month ago - By MedPageToday

    Betibeglogene autotemcel won FDA approval Wednesday as the first gene therapy for the treatment of adult and pediatric patients with beta-thalassemia who require regular red blood cell transfusions...
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  • FDA Approves First Gene Therapy for Beta-Thalassemia

    FDA Approves First Gene Therapy for Beta-Thalassemia

    1 month ago - By Medscape

    Betibeglogene autotemcel represents a potential cure for patients with beta-thalassemia, but the price tag is $2.1 million.
    FDA Approvals
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